Refer a patient.

Have a patient with metachromatic leukodystrophy whose family may be interested in the Embolden Study? The Embolden Study is evaluating the safety and effects of a study drug on gross motor function in children with late infantile MLD.

If you know a patient whose family may be interested, and you think he or she may qualify, refer your patient to any of the study sites listed. The research staff members will be able to answer any questions you may have about the study. Each patient will be required to have a visit with the study doctor to further evaluate if he or she may qualify.

Thank you for your interest in the Embolden Study.

To discuss the potential patient, please contact a site.


Dr. Barbara Burton

Ann & Robert H. Lurie Children's Hospital of Chicago
225 East Chicago Avenue
Chicago, Illinois 60611
Coordinator: Roxanne Del Rosario


Dr. Maria Escolar

Children's Hospital of Pittsburgh
4401 Penn Avenue
Plaza 407
Pittsburgh, Pennsylvania 15224
Coordinator: Jane Updyke