Who may qualify.
Infants and children who meet the following criteria, in addition to other criteria, may qualify for the Embolden Study:
- Is male or female six months to six years old
- Has been diagnosed with metachromatic leukodystrophy
- Has family that is willing and able to comply with the study instructions
Participation in the Embolden Study lasts approximately 112 weeks. During this time, you and your child will attend 110 study visits over four periods: the screening period, the surgery period, the treatment period, and the safety follow-up period.
Certain visits throughout the study will be completed at the main study site. Additional visits can be performed at a local site closer to your home. You will know which visits take place at the main site.